First Author /Principal Investigator | Year | Study Name/Identifier | Study Type | Disease Type | Age: Mean (SD) | Male Gender: N (%) |
---|---|---|---|---|---|---|
Benson [6] | 2018 | NEURO-TTR: NCT01737398 | RCT | ATTRv-PN | 60 (14) | 41 (68%) |
Berk [7] | 2013 | NA | RCT | ATTRv-PN | 59 (12) | 44 (67%) |
Coelho [8] | 2012 | FX005: NCT00409175 | RCT | ATTRv-PN | 38 (13) | 26 (43%) |
Hernandez-Ojeda [28] | 2012 | NA | RCT | DPN | 57 (9) | 6 (24%) |
Hor [29] | 2018 | NCT01973400 | RCT | DPN | 57 (9) | 63 (42%) |
Karama | 2020 | NA | Non-interventional study | CMT | 51 (13) | 6 (50%) |
DPN | 65 (11) | 4 (36%) | ||||
ATTRv-PN | 67 (7) | 9 (90%) | ||||
IPN | 66 (13) | 7 (58%) | ||||
Luigetti [30] | 2018 | NA | Non-interventional study | ATTRv-PN | 69 (9) | 15 (83%) |
Mundayat [31] | 2018 | THAOS | Non-interventional study | ATTRv-PN | 41 (9) | NA |
Sahenk [19] | 2005 | NA | RCT | CMT | 33 (5) | 3 (75%) |
Shy [32] | 2008 | NA | Non-interventional study | CMT | 40 (19) | 30 (42%) |
Tesfaye [33] | 2007 | Rochester Diabetic Neuropathy Study: NCT00044408 and NCT00044395 | RCT | DPN | 48 (9) | 115 (44%) |
Windebank [34] | 2004 | NA | RCT | Small fiber peripheral neuropathy | 62 (11) | NA |
Ziegler [35] | 1999 | ALADIN 3 | RCT | DPN | 57 (6) | 83 (50%) |
Ziegler [37] | 2009 | AV-007-IM: NCT00483730 | RCT | DPN | 56 (6) | 77 (27%) |
Ziegler [36] | 2011 | NATHAN 1: NCT00977483 | RCT | DPN | 54 (8) | 150 (67%) |