First Author/Principal Investigator | Year | Disease Type | Measure | Initial Assessment Scores | Rate of Change from Initial Assessment | |||||
---|---|---|---|---|---|---|---|---|---|---|
N | Mean | SD | Time Point | N | Mean | SE | ||||
Bensona [6] | 2018 | ATTRv-PN | NIS | 59 | 43.40 | 24.66 | 35 weeks | 56 | 7.98 | 1.32 |
66 weeks | 52 | 18.65 | 1.76 | |||||||
NIS-LL | 59 | 28.72 | 15.99 | 35 weeks | 56 | 3.66 | 0.76 | |||
66 weeks | 52 | 9.61 | 1.00 | |||||||
Berk [7] | 2013 | ATTRv-PN | NIS | 66 | 45.40 | 46.30 | 1 year | 37 | 10.10 | 1.63 |
2 years | 28 | 23.20 | 2.73 | |||||||
NIS-LL | 66 | 27.20 | 24.50 | 1 year | 37 | 6.00 | 1.10 | |||
2 years | 28 | 12.10 | 1.63 | |||||||
Coelho [8] | 2012 | ATTRv-PN | NIS-LL | 61 | 11.40 | 13.54 | 6 months | 57 | 2.05 | 0.66 |
12 months | 50 | 4.72 | 0.77 | |||||||
18 months | 47 | 5.83 | 0.92 | |||||||
Hernandez-Ojedab [28] | 2012 | DPN | NIS | 25 | 7.40 | 4.70 | 12 weeks | 25 | 0.70 | 1.15 |
Hor [29] | 2018 | DPN | NIS | 150 | 15.80 | 8.41 | 6 months | 150 | −3.30 | 0.54 |
12 months | 150 | −3.90 | 0.61 | |||||||
Karamc | 2020 | CMT | NIS | 12 | 59.79 | 24.22 | Annual rate of change from patients with various follow-up durations | 12 | 1.94 | 1.34 |
NIS-LL | 12 | 35.88 | 12.83 | 12 | 1.89 | 0.92 | ||||
DPN | NIS | 11 | 12.82 | 8.68 | 11 | 1.19 | 0.72 | |||
NIS-LL | 11 | 8.27 | 4.31 | 11 | 1.09 | 0.57 | ||||
ATTRv-PN | NIS | 10 | 29.15 | 29.91 | 10 | 18.31 | 4.41 | |||
NIS-LL | 10 | 15.95 | 14.00 | 10 | 9.35 | 1.70 | ||||
IPN | NIS | 12 | 34.35 | 22.78 | 12 | 0.42 | 0.99 | |||
NIS-LL | 12 | 24.25 | 14.06 | 12 | 0.43 | 0.39 | ||||
Luigetti [30] | 2018 | ATTRv-PN | NIS | 18 | 69.61 | 49.73 | 12 months | 13 | 6.50 | 1.38 |
24 months | 3 | 8.33 | 5.04 | |||||||
Mundayat [31] | 2018 | ATTRv-PN | NIS-LL | 167 | 7.57 | 7.29 | Annual rate of change over 2 years | 167 | 2.94 | 0.37 |
Sahenkb [19] | 2005 | CMT | NIS | 4 | 17.75 | 9.73 | 24 weeks | 4 | 1.25 | 5.20 |
Shy [32] | 2008 | CMT | NIS | 72 | 62.50 | 19.25 | Annual rate of change from patients with various follow-up durations | 72 | 1.37 | 0.38 |
Tesfaye [33] | 2007 | DPN | NIS-LL | 262 | 6.95 | 5.00 | 1 year | 211 | 0.63 | 0.23 |
Windebank [34] | 2004 | Small fiber peripheral neuropathy | NIS | NA | NA | NA | 6 months | 18 | −0.40 | 1.15 |
Ziegler [35] | 1999 | DPN | NIS | 165 | 14.00 | 10.40 | 7 months | 124 | −4.37 | 0.83 |
NIS-LL | 165 | 11.00 | 7.30 | 7 months | 125 | −3.37 | 0.54 | |||
Ziegler [37] | 2009 | DPN | NIS-LL | 286 | 8.80 | 7.30 | 160 days | 286 | −3.70 | 0.30 |
Ziegler [36] | 2011 | DPN | NIS | 224 | 12.20 | 7.80 | 2 years | 207 | 0.12 | 0.43 |
4 years | 207 | 0.61 | 0.46 | |||||||
NIS-LL | 224 | 9.50 | 5.30 | 2 years | 207 | 0.03 | 0.29 | |||
4 years | 207 | 0.43 | 0.31 |