Fig. 1

a HFMSE score in individual patients during risdiplam treatment. HFMSE – Hammersmith Functional Motor Scale – Expanded; For visibility purposes, the data for patient 3 has been excluded; this patient maintained an HFMSE score of 62 at both baseline and month 4. b RULM score in individual patients during risdiplam treatment. RULM – Revised Upper Limb Module; For visibility purposes, the data for patient 3 has been excluded; this patient maintained an RULM score of 37 at both baseline and month 4